spinal muscular atrophy (SMA) Archives

13 February 2024

SMA Gene Therapy Zolgensma Gets Orphan Medicine Status In Malaysia

Gene therapy Zolgensma – which has been registered to treat spinal muscular atrophy (SMA), a rare disease, in children aged below 2 years – receives Orphan Medicine status that enables NPRA priority review, so that patients can get fast access to the drug.

22 November 2023

Malaysia

THOMSON Hospital Celebrates Paediatric Excellence In Conjunction With World Children’s Day

Award-winning THOMSON Hospital Kota Damansara notched historic achievements in paediatrics this year, including performing its first Kasai and Myasthenia surgeries and being the first hospital in Southeast Asia to administer Spinraza to treat spinal muscular atrophy (SMA).

16 June 2022

Malaysia

Malaysia Approves First Drug To Treat SMA

The NPRA has authorised Roche’s Evrysdi for treatment of spinal muscular atrophy (SMA) in adults and children aged two months and older.

28 February 2022

Letter

SMA-LL Steps To Keep Moving Forward — Yap Sook Yee & Edmund Lim

There must be better understanding and support for people living with rare diseases in Malaysia.

13 August 2021

Letter

Children With SMA Must Not Be Left Behind — Azrul Mohd Khalib

The continued absence of effective treatments for SMA in Malaysia denies people with this condition the chance of living a different and better future.

1 June 2020

Letter

James Low: Lawyer, Law Scholar, Disability Rights Advocate, Child of God, Brother, Friend — Harapan OKU

James's one final wish would be for the Persons with Disabilities (PwD) Act 2008 to be reformed.

29 November 2019

Letter

One Step Forward By Ministry Of Health For SMA Patients

One Step Forward by the Ministry of Health with the National Framework for Rare Disease. Patients and families with Spinal Muscular Atrophy (SMA) in Malaysia are encouraged.

20 November 2019

Malaysia

MOH: Spinal Muscular Atrophy Drugs Not Yet Registered In Malaysia

There is also no database for SMA, says MOH.

8 October 2019

Malaysia

Budget 2020: Patients Want New Cancer Drugs, Rare Disease Funds

Increase allocations for public university hospitals, as most cancer patients there suffer financial catastrophe.

Tag: spinal muscular atrophy (SMA)

SMA Gene Therapy Zolgensma Gets Orphan Medicine Status In Malaysia

THOMSON Hospital Celebrates Paediatric Excellence In Conjunction With World Children’s Day

Malaysia Approves First Drug To Treat SMA

SMA-LL Steps To Keep Moving Forward — Yap Sook Yee & Edmund Lim

Children With SMA Must Not Be Left Behind — Azrul Mohd Khalib

James Low: Lawyer, Law Scholar, Disability Rights Advocate, Child of God, Brother, Friend — Harapan OKU

One Step Forward By Ministry Of Health For SMA Patients

MOH: Spinal Muscular Atrophy Drugs Not Yet Registered In Malaysia

Budget 2020: Patients Want New Cancer Drugs, Rare Disease Funds

Battling NCD Crisis Starts With Eating Right To Get To Healthy Weight

Don’t Fear Lawsuits From Performing CPR: IJN Doctor

Closed In Three Hospitals, MOH’s FPP Service Severely Cut Post-Pandemic

Dewan Rakyat Passes Controversial Act 342 Amendment Bill On Infectious Disease Control

IJN Seeks Up To 40% Fee Hike For Government Patients, Plans Diversification Beyond Cardiovascular